Synonyms:
Status: Phase 3
Entry Type: Protein
Molecule Category: UNKNOWN
UNII: OMD1OJM5L7

Pharmacology

Action Mechanism of Action Reference
EXOGENOUS PROTEIN Coagulation factor IX exogenous protein

Indications

Mesh Heading Maximum Phase Mesh ID Reference
Hemophilia B 3 D002836 ClinicalTrials
Ataxia Telangiectasia 2 D001260 ClinicalTrials
Sandhoff Disease 2 D012497 ClinicalTrials
Tay-Sachs Disease 2 D013661 ClinicalTrials
Niemann-Pick Disease, Type C 2 D052556 ClinicalTrials
Gangliosidoses, GM2 2 D020143 ClinicalTrials

Cross References

Resources Reference
ChEMBL CHEMBL3039538
FDA SRS OMD1OJM5L7