Synonyms:
Status: Phase 2
Entry Type: Oligonucleotide
Molecule Category: UNKNOWN
UNII: 7CAZ46X8EL

Pharmacology

Action Mechanism of Action Reference
POSITIVE MODULATOR CEP290 mRNA positive modulator

Indications

Mesh Heading Maximum Phase Mesh ID Reference
Leber Congenital Amaurosis 1 D057130 ClinicalTrials

Cross References

Resources Reference
ChEMBL CHEMBL4594497
FDA SRS 7CAZ46X8EL