| Synonyms: | |
| Status: | Phase 3 |
| Entry Type: | Gene |
| Molecule Category: | UNKNOWN |
| ATC: | B06AX02 |
| UNII: | MEE8487RTP |
| Action | Mechanism of Action | Reference |
|---|---|---|
| EXOGENOUS GENE | Hemoglobin beta chain exogenous gene |
| Mesh Heading | Maximum Phase | Mesh ID | Reference |
|---|---|---|---|
| beta-Thalassemia | 4 | D017086 | ClinicalTrials |
| Anemia, Sickle Cell | 1 | D000755 | ClinicalTrials |
| Resources | Reference |
|---|---|
| ChEMBL | CHEMBL4594311 |
| FDA SRS | MEE8487RTP |