Pharmacology

Action Mechanism of Action Reference
EXOGENOUS GENE Hemoglobin beta chain exogenous gene

Indications

Mesh Heading Maximum Phase Mesh ID Reference
beta-Thalassemia 4 D017086 ClinicalTrials
Anemia, Sickle Cell 1 D000755 ClinicalTrials

Cross References

Resources Reference
ChEMBL CHEMBL4594311
FDA SRS MEE8487RTP