Pharmacology

Action Mechanism of Action Reference
ANTISENSE INHIBITOR Transmembrane protease serine 6 mRNA antisense inhibitor

Indications

Mesh Heading Maximum Phase Mesh ID Reference
Polycythemia Vera 2 D011087 ClinicalTrials
beta-Thalassemia 2 D017086 ClinicalTrials
Thalassemia 1 D013789 ClinicalTrials

Cross References

Resources Reference
ChEMBL CHEMBL4650478
FDA SRS DXS4HJC32N