Display Options:
Total: 6532
Small molecule
Approved
Unknown
Unknown
Acne Vulgaris; Chalazion; Multiple Sclerosis; Multiple Sclerosis, Chronic Progressive; Multiple Sclerosis, Relapsing-Remitting; Osteomyelitis; Burns; Lyme Disease; Lymphoma, Non-Hodgkin; Candidiasis, Vulvovaginal; Conjunctivitis, Inclusion; Helicobacter Infections; Periodontitis; Vaginosis, Bacterial; Bacterial Infections; Eye Infections; Infections
Bacterial 70S ribosome inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
OTHER
INJECTION
Unknown
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections; Eye Infections
Bacterial dihydropteroate synthase inhibitor
Small molecule
Approved
OTHER
INJECTION; ORAL
Acquired Immunodeficiency Syndrome; Anemia; Blast Crisis; Brain Neoplasms; Chordoma; Genetic Diseases, Inborn; HIV Infections; Leukemia, Myeloid; Liver Neoplasms; Melanoma; Neoplasms, Germ Cell and Embryonal; Osteogenesis Imperfecta; Ovarian Neoplasms; Retinoblastoma; Wiskott-Aldrich Syndrome; X-Linked Combined Immunodeficiency Diseases; Adrenoleukodystrophy; Anemia, Sickle Cell; beta-Thalassemia; Breast Neoplasms, Male; Central Nervous System Neoplasms; Epidermolysis Bullosa; Fanconi Anemia; Fucosidosis; Gangliosidosis, GM1; Gaucher Disease; Glioma; Granulomatous Disease, Chronic; Hematologic Diseases; Hematologic Neoplasms; Hemoglobinopathies; Histiocytosis, Langerhans-Cell; Hodgkin Disease; Immune System Diseases; Immunologic Deficiency Syndromes; Inflammatory Breast Neoplasms; Kidney Neoplasms; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelomonocytic, Juvenile; Leukemia, Plasma Cell; Leukodystrophy, Globoid Cell; Leukodystrophy, Metachromatic; Lymphoma, AIDS-Related; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell; Myelodysplastic-Myeloproliferative Diseases; Myeloproliferative Disorders; Neoplasms, Plasma Cell; Neuronal Ceroid-Lipofuscinoses; Niemann-Pick Diseases; Osteopetrosis; Plasmacytoma; Primary Myelofibrosis; Sandhoff Disease; Severe Combined Immunodeficiency; Signs and Symptoms; Tay-Sachs Disease; Thalassemia; Wolman Disease; Anemia, Refractory; Anemia, Refractory, with Excess of Blasts; Breast Neoplasms; Ganglioneuroblastoma; Graft vs Host Disease; Leukemia, Basophilic, Acute; Leukemia, Erythroblastic, Acute; Leukemia, Megakaryoblastic, Acute; Leukemia, Monocytic, Acute; Leukemia, Myeloid, Acute; Leukemia, Myelomonocytic, Acute; Leukemia, Myelomonocytic, Chronic; Lymphoma; Multiple Myeloma; Myelodysplastic Syndromes; Neuroblastoma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Sarcoma; Sarcoma, Ewing; Thrombocythemia, Essential; Thrombosis; Hematopoietic Stem Cell Transplantation; Leukemia; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Neoplasms
DNA inhibitor
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease; Arthritis, Rheumatoid; Colitis, Ulcerative; Crohn Disease; Depressive Disorder, Major; Dermatitis, Atopic; Diabetes Mellitus; Diabetes Mellitus, Type 2; Epilepsy; Essential Hypertension; Hematologic Neoplasms; Hypertriglyceridemia; Ischemic Stroke; Lymphoma; Melanoma; Nausea; Neoplasm Metastasis; Neoplasms; Non-alcoholic Fatty Liver Disease; Obesity; Osteoarthritis, Knee; Pancreatic Neoplasms; Parkinson Disease; Prostatic Neoplasms; Psoriasis; Thrombophlebitis; Urinary Bladder, Overactive; Hemorrhage; Hypertension, Pulmonary; Liver Cirrhosis; Polyendocrinopathies, Autoimmune; Aortic Valve Stenosis; Atherosclerosis; Atrial Fibrillation; Atrial Flutter; Brain Infarction; Cardiovascular Diseases; Cerebral Infarction; Coronary Disease; Heart Diseases; Heart Failure; Idiopathic Pulmonary Fibrosis; Ischemic Attack, Transient; Multiple Sclerosis, Relapsing-Remitting; Myocardial Infarction; Myocardial Ischemia; Peripheral Vascular Diseases; Pregnancy; Prostatic Neoplasms, Castration-Resistant; Pulmonary Embolism; Rheumatic Heart Disease; Stroke; Thrombocytopenia; Thromboembolism; Venous Thromboembolism; Venous Thrombosis; Thrombosis
Unknown
Small molecule
Approved
OTHER
ORAL
Unknown
Nematode GABA-A receptor positive modulator
Small molecule
Approved
Unknown
Unknown
Hypotension; Pre-Eclampsia; Cardiovascular Diseases
Unknown
Small molecule
Approved
OTHER
ORAL
Stroke; Epilepsy; Seizures
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Cardiovascular Diseases; Heart Diseases; Hypertension
Adrenergic receptor alpha antagonist
Small molecule
Approved
Unknown
Unknown
Osteomyelitis; Hemorrhoids
Unknown
Small molecule
Approved
Unknown
Unknown
Digestive System Diseases
Unknown
Small molecule
Approved
CANCER; OTHER
INJECTION; ORAL; TOPICAL
Hematologic Neoplasms; Arthritis, Rheumatoid; Bronchiolitis Obliterans Syndrome; Crohn Disease; Epidermolysis Bullosa Acquisita; Pancreatic Neoplasms; Scleroderma, Diffuse; Sezary Syndrome; Graft vs Host Disease; Lymphoma; Mycosis Fungoides; Lymphoma, T-Cell; Psoriasis
DNA inhibitor
Small molecule
Approved
OTHER
INTRALYMPHATIC; INTRAUTERINE
Osteoarthritis, Knee; Carcinoma, Hepatocellular; Liver Neoplasms; Thrombosis; Neoplasms
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Hypersensitivity
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Cocaine-Related Disorders; Sciatica; Temporomandibular Joint Disorders; Parkinson Disease
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Dihydrofolate reductase inhibitor
Small molecule
Approved
Unknown
Unknown
Adenocarcinoma; Carcinoma, Renal Cell; Central Nervous System Neoplasms; Colitis, Ulcerative; Cystic Fibrosis; Glioma; Hepatitis C; Hepatitis C, Chronic; Hidradenitis Suppurativa; Insulin Resistance; Leukemia, Myeloid, Acute; Lung Diseases, Interstitial; Lymphangioleiomyomatosis; Melanoma; Multiple Myeloma; Myelodysplastic Syndromes; Neoplasms, Plasma Cell; Osteosarcoma; Ovarian Neoplasms; Prostatic Neoplasms; Retinitis Pigmentosa; Biliary Tract Neoplasms; Breast Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Cholangiocarcinoma; Colorectal Neoplasms; Communicable Diseases; Crohn Disease; Diabetes Mellitus, Type 1; Diabetes Mellitus, Type 2; Glioblastoma; Glomerulonephritis, IGA; Hearing Loss; HIV Infections; Leukemia; Leukemia, Lymphocytic, Chronic, B-Cell; Lichen Planus; Lung Neoplasms; Mastocytosis; Multiple Sclerosis, Chronic Progressive; Neoplasms; Osteoarthritis, Knee; Pancreatic Neoplasms; Porphyria Cutanea Tarda; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Small Cell Lung Carcinoma; Virus Diseases; Zellweger Syndrome; Abortion, Habitual; Antiphospholipid Syndrome; Arthritis, Rheumatoid; Coronavirus Infections; Giant Cell Arteritis; Graft vs Host Disease; Infections; Influenza, Human; Lupus Erythematosus, Cutaneous; Lupus Erythematosus, Systemic; Osteoarthritis; Pericarditis; Pneumonia; Pneumonia, Pneumocystis; Pneumonia, Viral; Polyendocrinopathies, Autoimmune; Pre-Eclampsia; Pregnancy; Respiratory Distress Syndrome; Respiratory Insufficiency; Sarcoidosis, Pulmonary; Severe Acute Respiratory Syndrome; Sjogren's Syndrome; Thrombocytopenia; Malaria
Unknown
Small molecule
Approved
Unknown
Unknown
Burkitt Lymphoma; Leukemia; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Large-Cell, Anaplastic; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Shock, Septic; Asthma
Glucocorticoid receptor agonist
Small molecule
Approved
MUSCULOSKELETAL; OTHER
ORAL
Anemia, Diamond-Blackfan; Canavan Disease; Diabetes Mellitus, Type 2; Esophageal Stenosis; Fanconi Anemia; Frontotemporal Dementia; Gangliosidoses; Gaucher Disease; Glucose Intolerance; Hematologic Diseases; Lymphoma, Primary Effusion; Respiratory Syncytial Virus Infections; Status Asthmaticus; Acquired Immunodeficiency Syndrome; Adrenal Insufficiency; AIDS-Associated Nephropathy; Amyotrophic Lateral Sclerosis; Anemia, Hemolytic, Autoimmune; Autoimmune Diseases; Bell Palsy; Blast Crisis; Blastic Plasmacytoid Dendritic Cell Neoplasm; Burkitt Lymphoma; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Castleman Disease; Chemical and Drug Induced Liver Injury; Churg-Strauss Syndrome; Embolism, Cholesterol; Gastrointestinal Stromal Tumors; Geographic Atrophy; Glomerulosclerosis, Focal Segmental; Graves Ophthalmopathy; Hearing Loss; Hearing Loss, Sensorineural; Hemangioma; Hematologic Neoplasms; Hemophilia A; Hepatitis, Alcoholic; Hepatitis, Autoimmune; Hepatitis C; HIV Infections; Hypersensitivity; IgA Vasculitis; Immunoblastic Lymphadenopathy; Immunoglobulin G4-Related Disease; Kidney Neoplasms; Lichen Planus, Oral; Lung Diseases; Lung Neoplasms; Lymphohistiocytosis, Hemophagocytic; Lymphoma, AIDS-Related; Lymphoma, B-Cell; Lymphoma, Large-Cell, Anaplastic; Lymphoma, T-Cell; Lymphoproliferative Disorders; Melanoma; Multiple Sclerosis, Relapsing-Remitting; Myelodysplastic Syndromes; Myeloproliferative Disorders; Nephritis, Interstitial; Neuromyelitis Optica; Opsoclonus-Myoclonus Syndrome; Pneumonia, Viral; Polycythemia Vera; Polyradiculoneuropathy, Chronic Inflammatory Demyelinating; Premature Birth; Primary Myelofibrosis; Pulmonary Fibrosis; Stiff-Person Syndrome; Takayasu Arteritis; Thrombocythemia, Essential; Thymus Neoplasms; Vestibular Neuronitis; Alzheimer Disease; Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis; Breast Neoplasms; Bronchiolitis Obliterans Syndrome; Cardiomyopathies; Central Nervous System Neoplasms; Cystic Fibrosis; Deafness; Giant Cell Arteritis; Glomerulonephritis, IGA; Glomerulonephritis, Membranous; Graft vs Host Disease; Granulomatosis with Polyangiitis; Heart Diseases; Heart Failure; Histiocytosis, Langerhans-Cell; Hodgkin Disease; Hypereosinophilic Syndrome; Idiopathic Pulmonary Fibrosis; Kidney Diseases; Kidney Failure, Chronic; Leukemia, Biphenotypic, Acute; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Lymphoid; Leukemia-Lymphoma, Adult T-Cell; Leukemia, Myeloid, Acute; Lupus Nephritis; Lymphoma, B-Cell, Marginal Zone; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Peripheral; Microscopic Polyangiitis; Multiple Myeloma; Muscular Dystrophy, Duchenne; Myasthenia Gravis; Nasal Polyps; Neoplasms, Plasma Cell; Neuroblastoma; Pain; Pemphigoid, Bullous; Pericarditis; Polymyalgia Rheumatica; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Pulmonary Disease, Chronic Obstructive; Purpura, Thrombotic Thrombocytopenic; Renal Insufficiency, Chronic; Retroperitoneal Fibrosis; Rhinitis, Allergic, Perennial; Sarcoidosis, Pulmonary; Sarcoma; Sciatica; Severe Acute Respiratory Syndrome; Sinusitis; Tuberculosis; Urticaria; Uveitis; Uveitis, Intermediate; Vasculitis; Waldenstrom Macroglobulinemia; Addison Disease; Adrenal Hyperplasia, Congenital; Anemia; Anemia, Aplastic; Anemia, Hemolytic; Arthritis; Arthritis, Gouty; Arthritis, Juvenile; Arthritis, Psoriatic; Arthritis, Rheumatoid; Asthma; Berylliosis; Brain Neoplasms; Bursitis; Chorioretinitis; Choroiditis; Colitis, Ulcerative; Conjunctivitis, Allergic; Crohn Disease; Dermatitis, Atopic; Dermatitis, Contact; Dermatitis, Exfoliative; Dermatitis Herpetiformis; Dermatitis, Seborrheic; Dermatomyositis; Endocrine System Diseases; Erythema Multiforme; Herpes Zoster Ophthalmicus; Hypercalcemia; Inflammation; Iridocyclitis; Iritis; Keratitis; Leukemia; Lupus Erythematosus, Systemic; Lymphoma; Multiple Sclerosis; Mycosis Fungoides; Myocarditis; Neoplasms; Nephrotic Syndrome; Ophthalmia, Sympathetic; Optic Neuritis; Osteoarthritis; Pemphigus; Peptic Ulcer; Pneumonia; Polymyositis; Psoriasis; Pulmonary Eosinophilia; Purpura, Thrombocytopenic, Idiopathic; Rhinitis, Allergic; Rhinitis, Allergic, Seasonal; Sarcoidosis; Serum Sickness; Spondylitis; Spondylitis, Ankylosing; Stevens-Johnson Syndrome; Synovitis; Tennis Elbow; Tenosynovitis; Thrombocytopenia; Thyroiditis, Subacute; Trichinellosis; Tuberculosis, Meningeal; Tuberculosis, Pulmonary; Uveitis, Posterior
Glucocorticoid receptor agonist
Small molecule
Approved
Unknown
ORAL
Cocaine-Related Disorders; Cognition; Attention Deficit Disorder with Hyperactivity
Dopamine transporter releasing agent
Small molecule
Approved
Unknown
Unknown
Diabetes Mellitus; Fibromyalgia; HIV Infections; Hypotension, Orthostatic; Muscular Atrophy, Spinal; Myasthenia Gravis
Unknown
Small molecule
Approved
Unknown
Unknown
Bipolar Disorder; Amphetamine-Related Disorders; Cocaine-Related Disorders; Multiple Sclerosis; Opioid-Related Disorders; Schizophrenia; Stress Disorders, Post-Traumatic; Stroke; Paraganglioma; Arteriosclerosis; Attention Deficit Disorder with Hyperactivity; Narcolepsy; Substance-Related Disorders
Dopamine transporter releasing agent
Small molecule
Approved
Unknown
Unknown
Pregnancy; Cataract; Pain
Unknown
Small molecule
Approved
OTHER
ORAL; TRANSDERMAL
Alcoholism; Hypotension, Orthostatic; Opioid-Related Disorders; Postoperative Complications; Amphetamine-Related Disorders; Brain Injuries; Chronic Pain; Cocaine-Related Disorders; Feeding and Eating Disorders; Parkinson Disease; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Stress Disorders, Post-Traumatic; Substance-Related Disorders; Alzheimer Disease; Anemia, Sickle Cell; Asthenia; Bipolar Disorder; Brain Neoplasms; Delirium; Dementia; Depressive Disorder; Depressive Disorder, Major; Fatigue; Hematologic Neoplasms; Multiple Sclerosis; Neoplasms; Tobacco Use Disorder; Attention Deficit Disorder with Hyperactivity; Narcolepsy
Dopamine transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Parkinson Disease
Unknown
Small molecule
Approved
OTHER
ORAL
Altitude Sickness
Dopamine D2 receptor antagonist
Small molecule
Approved
OTHER
ORAL
Breast Neoplasms; Hypogonadism; Neoplasms; Orchitis
Androgen Receptor agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Hypotension, Orthostatic; Lipoma; Orthostatic Intolerance; Atrial Fibrillation; Kidney Calculi; Cardiovascular Diseases; Lung Diseases, Obstructive
Unknown
Small molecule
Approved
OTHER
RECTAL
Cardiotoxicity; Multiple Myeloma; Genital Neoplasms, Female; Headache; Migraine Disorders; Nausea; Anxiety; Postoperative Nausea and Vomiting; Psychotic Disorders; Schizophrenia
Dopamine D2 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Dementia; Depressive Disorder; Schizophrenia; Anxiety
Unknown
Small molecule
Approved
OTHER
ORAL
Hypertension
Synaptic vesicular amine transporter inhibitor