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Total: 1496
Small molecule
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER
INJECTION; INTRACRANIAL
Hereditary Breast and Ovarian Cancer Syndrome; Leukemia, Plasma Cell; Lymphoma, T-Cell, Cutaneous; Mycosis Fungoides; Neuroblastoma; Sezary Syndrome; Brain Neoplasms; Colorectal Neoplasms; Gliosarcoma; Graft vs Host Disease; Hematologic Diseases; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, T-Cell, Peripheral; Melanoma; Multiple Sclerosis, Relapsing-Remitting; Myasthenia Gravis; Neoplasms, Plasma Cell; Neuromyelitis Optica; Opsoclonus-Myoclonus Syndrome; Ovarian Neoplasms; Polyradiculoneuropathy, Chronic Inflammatory Demyelinating; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Stiff-Person Syndrome; Breast Neoplasms; Central Nervous System Neoplasms; Leukemia; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Oligodendroglioma; Paraganglioma; Astrocytoma; Ependymoma; Glioblastoma; Glioma; Hodgkin Disease; Lymphoma, Non-Hodgkin; Medulloblastoma; Multiple Myeloma; Neoplasms
DNA inhibitor
Small molecule
Approved
OTHER
INJECTION
Unknown
Diagnostic agent
Small molecule
Approved
OTHER
OPHTHALMIC
Sturge-Weber Syndrome; Hemangioma; Macular Degeneration; Migraine Disorders; Telangiectasia, Hereditary Hemorrhagic; Varicose Ulcer; Wet Macular Degeneration; Wounds and Injuries; Exfoliation Syndrome; Melanoma; Paronychia; Cardiovascular Diseases; Glaucoma; Glaucoma, Open-Angle; Ocular Hypertension
Beta-1 adrenergic receptor antagonist
Small molecule
Approved
OTHER
OPHTHALMIC
Mycoses; Acanthamoeba Keratitis; Eye Infections; Infections
Ergosterol sequestering agent
Small molecule
Approved
OTHER
OPHTHALMIC; ORAL
Optic Neuropathy, Ischemic; Low Tension Glaucoma; Corneal Edema; Hemangioma; Hypertension, Portal; Glaucoma; Glaucoma, Open-Angle; Ocular Hypertension
Beta-1 adrenergic receptor antagonist
Small molecule
Approved
OTHER
ORAL
Breast Neoplasms; Carcinoma, Squamous Cell; Desmoid Tumors; Fragile X Syndrome; Leukemia, Myeloid, Acute; Melanoma; Adenomatous Polyposis Coli; Colorectal Neoplasms; Precancerous Conditions; Arthritis, Rheumatoid; Osteoarthritis; Rheumatic Diseases; Spondylitis
Cyclooxygenase inhibitor
Small molecule
Approved
OTHER
INJECTION
Sexual Dysfunction, Physiological; Diabetic Neuropathies; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Hypogonadism; Neoplasms; Orchitis
Androgen Receptor agonist
Small molecule
Approved
OTHER
INTRAVESICAL
HIV Infections; Melanoma; Neoplasms; Osteoarthritis; Contracture; Cystitis, Interstitial; Reflex, Abnormal; Urinary Bladder, Overactive; Urinary Incontinence; Urinary Incontinence, Urge; Arthralgia; Cystitis; Infections; Myalgia
Unknown
Small molecule
Approved
OTHER
ORAL
Substance-Related Disorders; Anxiety; Dementia; Depressive Disorder; Schizophrenia; Sleep Initiation and Maintenance Disorders
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
OTHER
INJECTION
Carcinoma, Basal Cell; Carcinoma, Endometrioid; Cystadenoma, Serous; Digestive System Neoplasms; Genital Neoplasms, Female; Kidney Diseases; Klatskin Tumor; Liver Diseases; Neoplasms, Cystic, Mucinous, and Serous; Neuroendocrine Tumors; Primary Myelofibrosis; Rhabdomyosarcoma; Xerostomia; Bile Duct Neoplasms; Carcinoid Tumor; Carcinoma, Islet Cell; Carcinoma, Large Cell; Carcinoma, Merkel Cell; Carcinoma, Neuroendocrine; Carcinoma, Pancreatic Ductal; Carcinoma, Renal Cell; Carcinoma, Verrucous; Digestive System Diseases; Esthesioneuroblastoma, Olfactory; Gastrointestinal Stromal Tumors; Glioblastoma; Glioma; Granuloma, Lethal Midline; Immunoblastic Lymphadenopathy; Kidney Neoplasms; Leukemia; Leukemia-Lymphoma, Adult T-Cell; Lymphoma, AIDS-Related; Lymphoma, Large-Cell, Anaplastic; Mesothelioma, Malignant; Myelodysplastic Syndromes; Nausea; Neoplasm Metastasis; Paraganglioma; Penile Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Salivary Gland Neoplasms; Thymoma; Thyroid Neoplasms; Tongue Neoplasms; Uveal Melanoma; Adenocarcinoma; Adenocarcinoma of Lung; Adrenal Cortex Neoplasms; Anemia; Anus Neoplasms; Biliary Tract Neoplasms; Brain Neoplasms; Breast Neoplasms; Carcinoma; Carcinoma, Embryonal; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Central Nervous System Neoplasms; Cholangiocarcinoma; Choriocarcinoma; Choroid Plexus Neoplasms; Colorectal Neoplasms; Endodermal Sinus Tumor; Endometrial Neoplasms; Ependymoma; Esophageal Neoplasms; Fallopian Tube Neoplasms; Gallbladder Neoplasms; Ganglioneuroblastoma; Gestational Trophoblastic Disease; Head and Neck Neoplasms; Hepatoblastoma; Hodgkin Disease; Hypopharyngeal Neoplasms; Inflammatory Breast Neoplasms; Laryngeal Neoplasms; Liver Neoplasms; Lung Neoplasms; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Peripheral; Malaria; Mediastinal Neoplasms; Medulloblastoma; Melanoma; Mesothelioma; Mouth Neoplasms; Mucositis; Multiple Myeloma; Nasopharyngeal Carcinoma; Nasopharyngeal Neoplasms; Neoplasms, Germ Cell and Embryonal; Neuroblastoma; Neuroectodermal Tumors, Primitive; Oropharyngeal Neoplasms; Osteosarcoma; Ovarian Neoplasms; Pancreatic Neoplasms; Paranasal Sinus Neoplasms; Peritoneal Neoplasms; Pharyngeal Neoplasms; Pleural Effusion; Postoperative Nausea and Vomiting; Retinoblastoma; Sarcoma; Seminoma; Sex Cord-Gonadal Stromal Tumors; Skin Neoplasms; Small Cell Lung Carcinoma; Squamous Cell Carcinoma of Head and Neck; Stomach Neoplasms; Stomatitis; Teratoma; Testicular Neoplasms; Thymus Neoplasms; Triple Negative Breast Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Urogenital Neoplasms; Uterine Cervical Neoplasms; Uterine Neoplasms; Vulvar Neoplasms; Neoplasms
DNA inhibitor
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
ORAL
Astrocytoma; Brain Injuries; Burkitt Lymphoma; Carcinoma, Non-Small-Cell Lung; Central Nervous System Neoplasms; Colorectal Neoplasms; Epilepsies, Partial; Lung Neoplasms; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Medulloblastoma; Melanoma; Nasopharyngeal Carcinoma; Neoplasms; Ovarian Neoplasms; Paraganglioma; Sarcoma; Shock; Urinary Bladder Neoplasms; Wounds and Injuries; Alopecia; Brain Neoplasms; Breast Neoplasms; Carcinoma, Squamous Cell; Ependymoma; Glioblastoma; Glioma; Head and Neck Neoplasms; HIV Infections; Leukemia; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Lymphoma; Myelodysplastic Syndromes; Neuralgia; Pancreatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Retinitis Pigmentosa; Small Cell Lung Carcinoma; Supranuclear Palsy, Progressive; Thyroid Neoplasms; Uveal Melanoma; Alcoholism; Alzheimer Disease; Anxiety; Autistic Disorder; Dementia; Depressive Disorder; Migraine Disorders; Muscular Atrophy, Spinal; Paraparesis, Tropical Spastic; Psychomotor Agitation; Schizophrenia; Status Epilepticus; Bipolar Disorder; Epilepsy; Epilepsy, Absence; Epilepsy, Complex Partial; Mitochondrial Diseases; Seizures
Succinate semialdehyde dehydrogenase inhibitor
Small molecule
Approved
OTHER
INJECTION; ORAL; TOPICAL
Attention Deficit Disorder with Hyperactivity; Carcinoma, Non-Small-Cell Lung; Central Nervous System Neoplasms; Crohn Disease; Familial Hypophosphatemic Rickets; Melanoma; Mouth Neoplasms; Neoplasms; Opioid-Related Disorders; Osteoporosis, Postmenopausal; Prediabetic State; Rickets, Hypophosphatemic; Acute Kidney Injury; Breast Neoplasms; Carcinoma, Basal Cell; Cholangiocarcinoma; Chronic Kidney Disease-Mineral and Bone Disorder; Diabetes Mellitus, Type 1; Hyperparathyroidism, Secondary; Hypertension; Klinefelter Syndrome; Lupus Erythematosus, Systemic; Myelodysplastic Syndromes; Pancreatic Neoplasms; Prostatic Neoplasms; Sepsis; Severe Acute Respiratory Syndrome; Adenomatous Polyposis Coli; Diabetic Nephropathies; Fibroma; Osteopetrosis; Osteoporosis; Prostatic Neoplasms, Castration-Resistant; Hypocalcemia; Hypoparathyroidism; Kidney Failure, Chronic; Psoriasis
Vitamin D receptor agonist
Protein
Approved
MUSCULOSKELETAL; OTHER; PREGNANCY AND GYNECOLOGY
INJECTION; NASAL
Bone Diseases, Metabolic; Menopause; Osteoporosis; Bone Resorption; Hypercalcemia; Osteitis Deformans; Osteoporosis, Postmenopausal; Parathyroid Diseases
Calcitonin receptor agonist
Small molecule
Approved
OTHER
INJECTION
Osteomyelitis
Bacterial penicillin-binding protein inhibitor
Protein
Approved
OTHER
INJECTION
Unknown
Unknown
Small molecule
Approved
OTHER
INJECTION
Obesity; Premenstrual Syndrome
Estrogen receptor alpha agonist
Small molecule
Approved
OTHER
INHALATION
Heart Diseases; Opioid-Related Disorders; Respiratory Distress Syndrome; Subarachnoid Hemorrhage; Substance-Related Disorders; Hernia, Inguinal; Respiratory Insufficiency; Severe Acute Respiratory Syndrome
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
OTHER
ORAL
Unknown
Adrenergic receptor alpha-1 antagonist
Protein
Approved
OTHER
INJECTION
Unknown
Unknown
Small molecule
Approved
OTHER
ORAL; TOPICAL
Carcinoma, Non-Small-Cell Lung; Lung Diseases; Pemphigoid, Benign Mucous Membrane; Pemphigus; Pulmonary Fibrosis; Rosacea; Sarcoidosis; Stroke; Fever; HIV Infections; Malaria; Malaria, Falciparum; Malaria, Vivax; Pneumonia, Pneumocystis; Severe Acute Respiratory Syndrome; Acne Vulgaris; Dermatitis Herpetiformis; Leprosy
Dihydropteroate synthase 1 inhibitor
Small molecule
Approved
OTHER
ORAL
Unknown
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
OTHER
TOPICAL
Unknown
Glucocorticoid receptor agonist
Protein
Approved
OTHER
INJECTION
Diabetes Mellitus
Insulin receptor agonist
Small molecule
Approved
OTHER
ORAL
Psychotic Disorders; Hypertension; Pheochromocytoma
Tyrosine 3-hydroxylase inhibitor
Small molecule
Approved
DERMATOLOGY; OTHER
ORAL; TOPICAL
Acne Vulgaris; Ovarian Neoplasms; Alopecia; Hypertension
Sulfonylurea receptor 2, Kir6.2 opener
Protein
Approved
OTHER
INJECTION
Unknown
Unknown
Small molecule
Approved
OTHER
ORAL
Asthma; Smoking Cessation; Hemangioma; Angina Pectoris; Cardiovascular Diseases; Hypertension; Myocardial Infarction; Stroke
Beta-1 adrenergic receptor antagonist
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections; Bronchitis, Chronic; Infections; Otitis Media; Pharyngitis; Pneumonia; Sprains and Strains; Tonsillitis; Urinary Tract Infections
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
OTHER
ORAL
Depressive Disorder
Dopamine receptor antagonist
Protein
Approved
OTHER
INJECTION
Unknown
Unknown
Small molecule
Approved
OTHER
ORAL
Prostatic Neoplasms, Castration-Resistant; Breast Neoplasms; Neoplasms
Cytochrome P450 11A1 inhibitor
Protein
Approved
OTHER
INJECTION
Diabetes Mellitus
Insulin receptor agonist
Small molecule
Approved
OTHER
ORAL
Helminthiasis
DNA inhibitor
Protein
Approved
OTHER
INJECTION; NASAL
Anorexia Nervosa; Arrhythmias, Cardiac; Attention Deficit Disorder with Hyperactivity; Depressive Disorder, Major; Diabetes Insipidus; Gastroparesis; Inflammation; Memory; Neurodevelopmental Disorders; Opioid-Related Disorders; Pre-Eclampsia; Psychotic Disorders; Sleep Apnea Syndromes; Aging; Atrophic Vaginitis; Atrophy; Autistic Disorder; Carcinoma, Intraductal, Noninfiltrating; Chronic Pain; Cocaine-Related Disorders; Depressive Disorder; Feeding and Eating Disorders; Fragile X Syndrome; Frontotemporal Dementia; Mental Disorders; Mood Disorders; Myocardial Infarction; Neuralgia; Obesity; Obsessive-Compulsive Disorder; Osteoarthritis; Osteoarthritis, Knee; Pain; Phobia, Social; Prader-Willi Syndrome; Severe Acute Respiratory Syndrome; Sexual Dysfunction, Physiological; Sleep Apnea, Obstructive; Stress Disorders, Post-Traumatic; Substance-Related Disorders; Substance Withdrawal Syndrome; Weight Gain; Alcoholism; Child Development Disorders, Pervasive; Dystocia; Myoma; Postpartum Hemorrhage; Schizophrenia; Tinnitus; Hemorrhage; Uterine Inertia
Oxytocin receptor agonist
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections
Bacterial DNA gyrase inhibitor