| Trade Names: | |
| Synonyms: | |
| Status: | Approved (2016) |
| Entry Type: | Oligonucleotide |
| Molecule Category: | Salt |
| UNII: | 4CHB7QQU1Q |
| Parent Compound: | NUSINERSEN |
| Action | Mechanism of Action | Reference |
|---|---|---|
| POSITIVE MODULATOR | SMN2 pre-mRNA positive modulator | FDA |
| Resources | Reference |
|---|---|
| ChEMBL | CHEMBL3833342 |
| FDA SRS | 4CHB7QQU1Q |