Trade Names:
Synonyms:
Status: Approved (2016)
Entry Type: Oligonucleotide
Molecule Category: Salt
UNII: 4CHB7QQU1Q
Parent Compound: NUSINERSEN

Pharmacology

Action Mechanism of Action Reference
POSITIVE MODULATOR SMN2 pre-mRNA positive modulator FDA

Indications

Mesh Heading Maximum Phase Mesh ID Reference
Muscular Atrophy, Spinal 4 D009134 FDA

Related Entries

Parent

Adverse Reactions

System Organ Classification (SOC)
Relative Frequency (%)
Respiratory, thoracic and mediastinal disorders
17.39
Nervous system disorders
14.25
Infections and infestations
11.63
General disorders and administration site conditions
10.98
Injury, poisoning and procedural complications
9.54
Gastrointestinal disorders
7.71
Musculoskeletal and connective tissue disorders
6.01
Investigations
5.23
Skin and subcutaneous tissue disorders
3.01
Metabolism and nutrition disorders
2.75
Psychiatric disorders
2.48

Cross References

Resources Reference
ChEMBL CHEMBL3833342
FDA SRS 4CHB7QQU1Q