| Synonyms: | |
| Status: | Approved (2016) |
| Entry Type: | Oligonucleotide |
| Molecule Category: | Parent |
| ATC: | M09AX07 |
| UNII: | 5Z9SP3X666 |
| Action | Mechanism of Action | Reference |
|---|---|---|
| POSITIVE MODULATOR | SMN2 pre-mRNA positive modulator | FDA |
| Mesh Heading | Maximum Phase | Mesh ID | Reference |
|---|---|---|---|
| Muscular Atrophy, Spinal | 3 | D009134 | ClinicalTrials |
| Resources | Reference |
|---|---|
| CAS NUMBER | 1258984-36-9 |
| ChEMBL | CHEMBL3301572 |
| FDA SRS | 5Z9SP3X666 |
| Guide to Pharmacology | 9416 |