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ENT (5)
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NEUROLOGY DRUGS & NERVOUS SYSTEM (50)
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OTHER (1482)
Therapeutic Indication
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Display Options:
Drug type
Therapeutic Area
Route of administration
Mechanism of Action
Indication
Status
Total:
6532
DANICOPAN
2024
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Glomerulonephritis, Membranoproliferative; Hemoglobinuria, Paroxysmal
Complement factor D inhibitor
DANICOPAN
×
Maximum Phase:
4
First Approval:
2024
UNII:
JM8C1SFX0U
Molecule Type:
Small molecule
Molecular Formula:
C26H23BrFN7O3
Molecular Weight:
580.42
AlogP:
3.74
PSA:
122.97
HBD:
1.0
HBA:
#RotB:
6.0
Source:
ENSARTINIB
2024
Small molecule
Approved
Unknown
Unknown
Lung Neoplasms; Melanoma; Carcinoma, Non-Small-Cell Lung
ALK tyrosine kinase receptor inhibitor
ENSARTINIB
×
Maximum Phase:
4
First Approval:
2024
UNII:
SMA5ZS5B22
Molecule Type:
Small molecule
Molecular Formula:
C26H27Cl2FN6O3
Molecular Weight:
561.45
AlogP:
4.72
PSA:
122.47
HBD:
3.0
HBA:
#RotB:
6.0
Source:
REPOTRECTINIB
2024
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Neoplasms
Unknown
REPOTRECTINIB
×
Maximum Phase:
4
First Approval:
2024
UNII:
08O3FQ4UNP
Molecule Type:
Small molecule
Molecular Formula:
C18H18FN5O2
Molecular Weight:
355.37
AlogP:
2.55
PSA:
80.55
HBD:
2.0
HBA:
#RotB:
0.0
Source:
TREOSULFAN
2025
Small molecule
Investigational
Unknown
Unknown
Multiple Myeloma; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Graft vs Host Disease; Hematologic Neoplasms; Hodgkin Disease; Lymphoma, Non-Hodgkin; Leukemia, Myeloid, Acute; Melanoma; Myelodysplastic Syndromes; Ovarian Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Sarcoma, Ewing; Neoplasms
Unknown
TREOSULFAN
×
Maximum Phase:
3
First Approval:
2025
UNII:
CO61ER3EPI
Molecule Type:
Small molecule
Molecular Formula:
C6H14O8S2
Molecular Weight:
278.3
AlogP:
-2.34
PSA:
127.2
HBD:
2.0
HBA:
#RotB:
7.0
Source:
MIRDAMETINIB
2025
Small molecule
Approved
Unknown
Unknown
Colorectal Neoplasms; Neoplasms; Carcinoma, Non-Small-Cell Lung; Neurofibromatosis 1
Dual specificity mitogen-activated protein kinase kinase 1 inhibitor
MIRDAMETINIB
×
Maximum Phase:
4
First Approval:
2025
UNII:
86K0J5AK6M
Molecule Type:
Small molecule
Molecular Formula:
C16H14F3IN2O4
Molecular Weight:
482.2
AlogP:
2.47
PSA:
90.82
HBD:
4.0
HBA:
#RotB:
7.0
Source:
CYTOCHLOR
1
Small molecule
Investigational
Unknown
Unknown
Central Nervous System Neoplasms; Head and Neck Neoplasms
Unknown
CYTOCHLOR
×
Maximum Phase:
1
First Approval:
None
UNII:
J14D49ZN55
Molecule Type:
Small molecule
Molecular Formula:
C9H12ClN3O4
Molecular Weight:
261.67
AlogP:
-0.88
PSA:
110.6
HBD:
3.0
HBA:
#RotB:
2.0
Source:
ILX23-7553
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Vitamin D receptor agonist
ILX23-7553
×
Maximum Phase:
1
First Approval:
None
UNII:
O13QTC8612
Molecule Type:
Small molecule
Molecular Formula:
C27H38O3
Molecular Weight:
410.6
AlogP:
4.85
PSA:
60.69
HBD:
3.0
HBA:
#RotB:
3.0
Source:
BTA-9881
1
Small molecule
Investigational
Unknown
Unknown
Respiratory Syncytial Virus Infections
Unknown
BTA-9881
×
Maximum Phase:
1
First Approval:
None
UNII:
9VR1J6U4XG
Molecule Type:
Small molecule
Molecular Formula:
C21H15ClN4O2
Molecular Weight:
390.83
AlogP:
2.94
PSA:
66.4
HBD:
0.0
HBA:
#RotB:
2.0
Source:
NACUBACTAM
1
Small molecule
Investigational
Unknown
Unknown
Gram-Negative Bacterial Infections; Kidney Diseases; Urinary Tract Infections
Unknown
NACUBACTAM
×
Maximum Phase:
1
First Approval:
None
UNII:
832O37V7MZ
Molecule Type:
Small molecule
Molecular Formula:
C9H16N4O7S
Molecular Weight:
324.32
AlogP:
-2.0
PSA:
151.5
HBD:
3.0
HBA:
#RotB:
6.0
Source:
H-100
1
Small molecule
Investigational
Unknown
Unknown
Penile Induration
Unknown
H-100
×
Maximum Phase:
1
First Approval:
None
UNII:
None
Molecule Type:
Small molecule
Molecular Formula:
C11H11N3O3
Molecular Weight:
233.23
AlogP:
0.44
PSA:
102.22
HBD:
3.0
HBA:
#RotB:
5.0
Source:
GSK159802
1
Small molecule
Investigational
Unknown
Unknown
Pulmonary Disease, Chronic Obstructive
Beta-2 adrenergic receptor agonist
GSK159802
×
Maximum Phase:
1
First Approval:
None
UNII:
None
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
HKI-357
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
HKI-357
×
Maximum Phase:
1
First Approval:
None
UNII:
39R3638KZ6
Molecule Type:
Small molecule
Molecular Formula:
C31H29ClFN5O3
Molecular Weight:
574.06
AlogP:
6.68
PSA:
99.51
HBD:
2.0
HBA:
#RotB:
11.0
Source:
CT-1578
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Macrophage colony stimulating factor receptor inhibitor
CT-1578
×
Maximum Phase:
1
First Approval:
None
UNII:
None
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
NV-5138
1
Small molecule
Investigational
Unknown
Unknown
Depressive Disorder, Treatment-Resistant
Unknown
NV-5138
×
Maximum Phase:
1
First Approval:
None
UNII:
None
Molecule Type:
Small molecule
Molecular Formula:
C7H13F2NO2
Molecular Weight:
181.18
AlogP:
1.08
PSA:
63.32
HBD:
2.0
HBA:
#RotB:
4.0
Source:
PROPYL GALLATE
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
PROPYL GALLATE
×
Maximum Phase:
1
First Approval:
None
UNII:
8D4SNN7V92
Molecule Type:
Small molecule
Molecular Formula:
C10H12O5
Molecular Weight:
212.2
AlogP:
1.37
PSA:
86.99
HBD:
3.0
HBA:
#RotB:
3.0
Source:
PLX8394
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
PLX8394
×
Maximum Phase:
1
First Approval:
None
UNII:
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
KL-1333
1
Small molecule
Investigational
Unknown
Unknown
MELAS Syndrome; Mitochondrial Diseases
Unknown
KL-1333
×
Maximum Phase:
1
First Approval:
None
UNII:
NA2ZOL5UGM
Molecule Type:
Small molecule
Molecular Formula:
C14H12N2O2
Molecular Weight:
240.26
AlogP:
2.58
PSA:
62.82
HBD:
1.0
HBA:
#RotB:
1.0
Source:
CAFUSERTIB
1
Small molecule
Investigational
Unknown
Unknown
Leukemia, Myeloid, Acute; Neoplasms
Serine/threonine-protein kinase PLK1 inhibitor
CAFUSERTIB
×
Maximum Phase:
1
First Approval:
None
UNII:
None
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
LISAVANBULIN
1
Small molecule
Investigational
Unknown
Unknown
Glioblastoma; Neoplasms
Unknown
LISAVANBULIN
×
Maximum Phase:
1
First Approval:
None
UNII:
5PT0QP06X5
Molecule Type:
Small molecule
Molecular Formula:
C26H29N9O3
Molecular Weight:
515.58
AlogP:
2.69
PSA:
190.77
HBD:
4.0
HBA:
#RotB:
13.0
Source:
BETA-CARYOPHYLLENE
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
BETA-CARYOPHYLLENE
×
Maximum Phase:
1
First Approval:
None
UNII:
BHW853AU9H
Molecule Type:
Small molecule
Molecular Formula:
C15H24
Molecular Weight:
204.36
AlogP:
4.73
PSA:
0.0
HBD:
0.0
HBA:
#RotB:
0.0
Source:
ITX-5061
1
Small molecule
Investigational
Unknown
Unknown
Hepatitis C
Unknown
ITX-5061
×
Maximum Phase:
1
First Approval:
None
UNII:
J4RA8K2Q2A
Molecule Type:
Small molecule
Molecular Formula:
C30H38ClN3O7S
Molecular Weight:
620.17
AlogP:
4.05
PSA:
123.27
HBD:
2.0
HBA:
#RotB:
10.0
Source:
LB-102
1
Small molecule
Investigational
Unknown
Unknown
Schizophrenia
Unknown
LB-102
×
Maximum Phase:
1
First Approval:
None
UNII:
N81WKW91XF
Molecule Type:
Small molecule
Molecular Formula:
C18H29N3O4S
Molecular Weight:
383.51
AlogP:
1.74
PSA:
87.74
HBD:
2.0
HBA:
#RotB:
8.0
Source:
RG7893
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Sodium channel protein type IX alpha subunit blocker
RG7893
×
Maximum Phase:
1
First Approval:
None
UNII:
None
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
GSK-369796
1
Small molecule
Investigational
Unknown
Unknown
Malaria
Unknown
GSK-369796
×
Maximum Phase:
1
First Approval:
None
UNII:
None
Molecule Type:
Small molecule
Molecular Formula:
C20H22ClN3O
Molecular Weight:
355.87
AlogP:
5.23
PSA:
57.18
HBD:
3.0
HBA:
#RotB:
4.0
Source:
BGT226
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
BGT226
×
Maximum Phase:
1
First Approval:
None
UNII:
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
TELENZEPINE
1
Small molecule
Investigational
Unknown
Unknown
Obesity
Unknown
TELENZEPINE
×
Maximum Phase:
1
First Approval:
None
UNII:
0990EG3K10
Molecule Type:
Small molecule
Molecular Formula:
C19H22N4O2S
Molecular Weight:
370.48
AlogP:
2.53
PSA:
55.89
HBD:
1.0
HBA:
#RotB:
2.0
Source:
CIS-UROCANIC ACID
1
Small molecule
Investigational
Unknown
Unknown
Dry Eye Syndromes
Unknown
CIS-UROCANIC ACID
×
Maximum Phase:
1
First Approval:
None
UNII:
5LM7WD7VIC
Molecule Type:
Small molecule
Molecular Formula:
C6H6N2O2
Molecular Weight:
138.13
AlogP:
0.51
PSA:
65.98
HBD:
2.0
HBA:
#RotB:
2.0
Source:
IMD-2560
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Inhibitor of nuclear factor kappa B kinase beta subunit inhibitor
IMD-2560
×
Maximum Phase:
1
First Approval:
None
UNII:
None
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
DELANZOMIB
1
Small molecule
Investigational
Unknown
Unknown
Lymphoma, Non-Hodgkin; Multiple Myeloma
Unknown
DELANZOMIB
×
Maximum Phase:
1
First Approval:
None
UNII:
6IF28942WO
Molecule Type:
Small molecule
Molecular Formula:
C21H28BN3O5
Molecular Weight:
413.28
AlogP:
None
PSA:
None
HBD:
None
HBA:
#RotB:
None
Source:
BMS-214662
1
Small molecule
Investigational
Unknown
Unknown
Anemia, Refractory, with Excess of Blasts; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Promyelocytic, Acute; Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma
Unknown
BMS-214662
×
Maximum Phase:
1
First Approval:
None
UNII:
L2U9GFD244
Molecule Type:
Small molecule
Molecular Formula:
C25H23N5O2S2
Molecular Weight:
489.63
AlogP:
4.17
PSA:
93.09
HBD:
1.0
HBA:
#RotB:
6.0
Source:
FENAMIC ACID
1
Small molecule
Investigational
Unknown
Unknown
Pancreatic Neoplasms
Unknown
FENAMIC ACID
×
Maximum Phase:
1
First Approval:
None
UNII:
952VN06WBB
Molecule Type:
Small molecule
Molecular Formula:
C13H11NO2
Molecular Weight:
213.24
AlogP:
3.13
PSA:
49.33
HBD:
2.0
HBA:
#RotB:
3.0
Source:
PF-03882845
1
Small molecule
Investigational
Unknown
Unknown
Diabetes Mellitus, Type 2; Diabetic Nephropathies
Mineralocorticoid receptor antagonist
PF-03882845
×
Maximum Phase:
1
First Approval:
None
UNII:
34ZKU73FU3
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
EPZ-5676
1
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
EPZ-5676
×
Maximum Phase:
1
First Approval:
None
UNII:
Molecule Type:
Small molecule
Molecular Formula:
Molecular Weight:
AlogP:
PSA:
HBD:
HBA:
#RotB:
Source:
HYPERICIN
1
Small molecule
Investigational
Unknown
Unknown
HIV Infections; Lymphoma, T-Cell, Cutaneous
Unknown
HYPERICIN
×
Maximum Phase:
1
First Approval:
None
UNII:
7V2F1075HD
Molecule Type:
Small molecule
Molecular Formula:
C30H16O8
Molecular Weight:
504.45
AlogP:
5.08
PSA:
155.52
HBD:
6.0
HBA:
#RotB:
0.0
Source:
BMS-984923
1
Small molecule
Investigational
Unknown
Unknown
Alzheimer Disease
Unknown
BMS-984923
×
Maximum Phase:
1
First Approval:
None
UNII:
3I1803DK5Z
Molecule Type:
Small molecule
Molecular Formula:
C22H15ClN2O2
Molecular Weight:
374.83
AlogP:
4.66
PSA:
51.22
HBD:
1.0
HBA:
#RotB:
2.0
Source:
1
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Molecular Weight
ALogP
PSA