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Total: 6532
Small molecule
Approved
OTHER
ORAL
Cataract; Diabetes Mellitus
Sulfonylurea receptor 1, Kir6.2 blocker
Small molecule
Approved
OTHER
INJECTION; ORAL
Aortic Diseases; Craniosynostoses; Rosacea; Inflammation; Hemorrhage
Plasminogen inhibitor
Small molecule
Approved
OTHER
ORAL
Anemia; beta-Thalassemia; Blast Crisis; Central Nervous System Neoplasms; Chordoma; Crohn Disease; Fallopian Tube Neoplasms; Glioma; Hereditary Breast and Ovarian Cancer Syndrome; Immune System Diseases; Leukemia, Lymphoid; Neoplasms, Germ Cell and Embryonal; Neoplasms, Neuroepithelial; Oligodendroglioma; Peritoneal Neoplasms; Adenoma, Islet Cell; Anemia, Aplastic; Anemia, Diamond-Blackfan; Brain Neoplasms; Breast Neoplasms, Male; Bronchiectasis; Burkitt Lymphoma; Carcinoma, Neuroendocrine; Carcinoma, Renal Cell; Graft vs Host Disease; Granuloma, Lethal Midline; Hematologic Diseases; Hematologic Neoplasms; Hemoglobinuria; Histiocytosis; Histiocytosis, Langerhans-Cell; Hodgkin Disease; Immunoblastic Lymphadenopathy; Inflammatory Breast Neoplasms; Kidney Neoplasms; Leukemia, Erythroblastic, Acute; Leukemia, Large Granular Lymphocytic; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia-Lymphoma, Adult T-Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myelomonocytic, Chronic; Leukemia, Myelomonocytic, Juvenile; Leukemia, Plasma Cell; Liver Neoplasms; Lymphoma, B-Cell, Marginal Zone; Lymphoma, Large-Cell, Anaplastic; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell; Lymphoma, T-Cell, Peripheral; Medulloblastoma; Multiple Sclerosis, Relapsing-Remitting; Myasthenia Gravis; Mycosis Fungoides; Myelodysplastic-Myeloproliferative Diseases; Myeloproliferative Disorders; Neuromyelitis Optica; Opsoclonus-Myoclonus Syndrome; Plasmacytoma; Polycythemia Vera; Polyradiculoneuropathy, Chronic Inflammatory Demyelinating; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Primary Myelofibrosis; Prostatic Neoplasms, Castration-Resistant; Retinal Neoplasms; Severe Combined Immunodeficiency; Sezary Syndrome; Shwachman-Diamond Syndrome; Stiff-Person Syndrome; Testicular Neoplasms; Thalassemia; Waldenstrom Macroglobulinemia; Wiskott-Aldrich Syndrome; Amyloidosis, Familial; Anemia, Sickle Cell; Breast Neoplasms; Colorectal Neoplasms; Ganglioneuroblastoma; Immunoglobulin Light-chain Amyloidosis; Leukemia; Leukemia, Myeloid, Acute; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Melanoma; Myelodysplastic Syndromes; Neoplasms, Plasma Cell; Neuroblastoma; Ovarian Neoplasms; Retinoblastoma; Sarcoma; Sarcoma, Ewing; Smoldering Multiple Myeloma; Uveal Melanoma; Carcinoma; Multiple Myeloma; Neoplasms
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Psoriasis
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections
Bacterial DNA gyrase inhibitor
Small molecule
Approved
OTHER
ORAL
Anxiety; Osteomyelitis; Pulmonary Disease, Chronic Obstructive; Sleep Apnea Syndromes; Spinal Cord Injuries; Tourette Syndrome; Agoraphobia; Alcohol Drinking; Bipolar Disorder; Brain Injuries; Cocaine-Related Disorders; Depressive Disorder, Major; Fibromyalgia; Low Back Pain; Motor Activity; Opioid-Related Disorders; Psychotic Disorders; Pyelonephritis; Stroke; Substance-Related Disorders; Tobacco Use Disorder; Asperger Syndrome; Autistic Disorder; Obsessive-Compulsive Disorder; Pain; Panic Disorder; Phobia, Social; Phobic Disorders; Schizophrenia; Smoking Cessation; Stress Disorders, Post-Traumatic; Tuberculosis, Pulmonary; Tuberculosis
Alanine racemase inhibitor
Small molecule
Approved
OTHER
ORAL
Atherosclerosis; Coronary Disease; Death, Sudden, Cardiac; Diabetes Mellitus, Type 2; Hypercholesterolemia; Cardiovascular Diseases; Edema; Heart Failure; Hyperaldosteronism; Hypertension; Liver Cirrhosis; Nephrotic Syndrome; Toxemia
Amiloride-sensitive sodium channel, ENaC blocker
Small molecule
Approved
Unknown
Unknown
Osteomyelitis; Bacterial Infections; Multiple Sclerosis
Bacterial 70S ribosome inhibitor
Small molecule
Approved
Unknown
Unknown
Clostridium Infections; Cystic Fibrosis; Abscess; Bacterial Infections; Cellulitis; Cross Infection; Skin Diseases; Staphylococcal Skin Infections; Endocarditis; Infections
Peptidoglycan inhibitor
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Acne Vulgaris; Bacterial Infections; Eye Infections; Infections
Bacterial 70S ribosome inhibitor
Small molecule
Approved
Unknown
Unknown
Poisoning; Organophosphate Poisoning
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Child Development Disorders, Pervasive; Melanoma; Multiple Sclerosis; Osteoarthritis; Peritonitis; Prostatic Neoplasms, Castration-Resistant; Renal Insufficiency; Sinusitis; Carcinoma, Hepatocellular; Colitis, Ulcerative; Constipation; Crohn Disease; Cystic Fibrosis; Fractures, Bone; Graft vs Host Disease; Hematologic Neoplasms; Joint Diseases; Neonatal Sepsis; Obesity; Pneumonia, Staphylococcal; Pneumonia, Ventilator-Associated; Postoperative Complications; Prediabetic State; Renal Insufficiency, Chronic; Wounds and Injuries; Abscess; Bacteremia; Cellulitis; Cholangitis, Sclerosing; Clostridium Infections; Conjunctivitis, Bacterial; Cross Infection; Diabetic Foot; Gram-Positive Bacterial Infections; Infections; Inflammation; Osteomyelitis; Pneumonia; Pneumonia, Bacterial; Staphylococcal Infections; Staphylococcal Skin Infections; Bacterial Infections; Diarrhea; Endocarditis; Enterocolitis; Eye Infections; Respiratory Tract Infections; Sepsis; Skin Diseases
Peptidoglycan inhibitor
Small molecule
Approved
OTHER
FOR RX COMPOUNDING; OPHTHALMIC; ORAL; TOPICAL
Erectile Dysfunction; Hepatitis C; Leukemia, Lymphocytic, Chronic, B-Cell; Osteomyelitis; Renal Insufficiency; Bulimia Nervosa; Colorectal Neoplasms; Feeding and Eating Disorders; Gastroparesis; Pulmonary Disease, Chronic Obstructive; Stomach Neoplasms; Carcinoma, Non-Small-Cell Lung; Chlamydia Infections; Epidermolysis Bullosa; Gastrointestinal Hemorrhage; Hematemesis; HIV Infections; Pneumonia; Acne Vulgaris; Bacterial Infections; Eye Infections; Infections; Whooping Cough
Bacterial 70S ribosome inhibitor
Small molecule
Approved
OTHER
ORAL; TOPICAL; VAGINAL
Dental Caries; Kidney Diseases; Macular Degeneration; Bacteremia; Burns; Graft vs Host Disease; Pneumonia; Stomatitis, Denture; Candidiasis, Oral; HIV Infections; Leukemia; Lymphoma; Multiple Myeloma; Myelodysplastic Syndromes; Myeloproliferative Disorders; Stomatitis; Tobacco Use Disorder; Vaginosis, Bacterial; Candidiasis; Infections
Ergosterol sequestering agent
Small molecule
Approved
OTHER
ORAL
Unknown
Androgen Receptor agonist
Small molecule
Approved
OTHER
INJECTION; ORAL; TOPICAL
Leishmaniasis, Cutaneous; Aspergillosis, Allergic Bronchopulmonary; Candidiasis, Chronic Mucocutaneous; Candidiasis, Invasive; Fuchs' Endothelial Dystrophy; Intracranial Hypertension; Leukemia, Myeloid, Acute; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Blastomycosis; Candidiasis, Vulvovaginal; Leishmaniasis; Leishmaniasis, Mucocutaneous; Leukemia; Lung Diseases; Lymphoma; Multiple Myeloma; Myelodysplastic Syndromes; Myeloproliferative Disorders; Neoplasms; Pulmonary Aspergillosis; Vaginosis, Bacterial; Aspergillosis; Candidiasis; Cryptococcosis; Histoplasmosis; Infections; Leishmaniasis, Visceral; Meningitis, Cryptococcal; Mucormycosis; Mycoses; Sporotrichosis; Zygomycosis
Ergosterol sequestering agent
Small molecule
Approved
OTHER
TOPICAL
Kidney Failure, Chronic; Skin Diseases
Glucocorticoid receptor agonist
Small molecule
Approved
Unknown
Unknown
Bacteremia; Gram-Positive Bacterial Infections; Infections; Osteomyelitis; Bacterial Infections
Unknown
Small molecule
Approved
Unknown
Unknown
Fasciitis, Plantar; Pregnancy
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoma, Squamous Cell; Chronic Pain; Keratosis, Actinic; Neuralgia, Postherpetic; Pregnancy; Premature Ejaculation; Skin Diseases; Pain
Sodium channel alpha subunit blocker
Small molecule
Approved
OTHER
ORAL
HIV Infections; Tobacco Use Disorder; Dementia; Depressive Disorder; Schizophrenia; Anxiety; Anxiety Disorders; Mental Disorders
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Dystonic Disorders; Osteomyelitis; Chorioamnionitis; Cleft Palate; Kidney Calculi; Premature Birth; Sepsis; Bacterial Infections; Eye Infections; Gonorrhea; Infections; Meningitis
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
Unknown
Unknown
Central Nervous System Neoplasms; Brain Neoplasms; Carcinoma, Renal Cell; Constriction, Pathologic; Glioma; Leukemia, Myeloid, Acute; Neurofibromatosis 1; Paraganglioma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Histiocytosis, Langerhans-Cell; Hodgkin Disease; Leukemia; Lung Neoplasms; Lymphoma; Lymphoma, Large B-Cell, Diffuse; Lymphoma, T-Cell, Peripheral; Melanoma; Prostatic Neoplasms, Castration-Resistant; Skin Neoplasms; Testicular Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Low Back Pain; Osteoarthritis; Tendinopathy; Anemia; Asthma; Colitis, Ulcerative; Dermatitis; Nephrotic Syndrome; Serum Sickness
Glucocorticoid receptor agonist
Small molecule
Approved
OTHER
INJECTION
Cystic Fibrosis; Neoplasms; Pain; Cataract; Malaria; Urinary Tract Infections; Acidosis
Unknown
Small molecule
Approved
Unknown
Unknown
Panic Disorder; Respiratory Tract Diseases
Unknown
Small molecule
Approved
OTHER
ORAL
Pancreatic Neoplasms
Unknown
Small molecule
Approved
OTHER
INHALATION; INJECTION; INTRAMUSCULAR; INTRAOCULAR; INTRAVENOUS; SUBCUTANEOUS
Anaphylaxis; Chronic Pain; Depressive Disorder; Diabetes Mellitus; Infections; Parathyroid Neoplasms; Skin Neoplasms; Tachypnea; Acute Lung Injury; Appendicitis; Breast Neoplasms; Cognitive Dysfunction; Death, Sudden, Cardiac; Hemoptysis; Hypospadias; Hypotension; Leukemia, Hairy Cell; Musculoskeletal Diseases; Rotator Cuff Injuries; Sepsis; Shock; Tachycardia, Ventricular; Ventricular Fibrillation; Wounds and Injuries; Bronchiolitis; Carcinoma, Non-Small-Cell Lung; Epistaxis; Fractures, Bone; Gastrointestinal Hemorrhage; Genital Neoplasms, Male; Heart Failure; Lung Neoplasms; Myoma; Osteoarthritis, Knee; Pain; Pulpitis; Rhinitis, Allergic, Perennial; Stomach Neoplasms; Stroke; Angioedema; Asthma; Bronchial Spasm; Cardiovascular Diseases; Glaucoma; Heart Arrest; Hemorrhage; Hypersensitivity; Lung Diseases, Obstructive; Muscle Cramp; Mydriasis; Nasal Obstruction; Rhinitis, Allergic, Seasonal; Serum Sickness; Shock, Septic; Sinusitis; Urticaria
Adrenergic receptor agonist
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Tuberculosis, Multidrug-Resistant; Tuberculosis, Pulmonary; Tuberculosis
Enoyl-[acyl-carrier-protein] reductase inhibitor
Small molecule
Approved
Unknown
Unknown
Asthma; Breast Neoplasms; Colitis, Ulcerative; Hypotension, Orthostatic; Lecithin Cholesterol Acyltransferase Deficiency; Pancreatitis, Chronic; Carcinoma, Squamous Cell; Histiocytosis, Langerhans-Cell; Melanoma; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Squamous Intraepithelial Lesions; Toothache; Alzheimer Disease; Hemorrhage; Inflammation; Pancreatitis; Premature Birth; Renal Colic; Severe Acute Respiratory Syndrome; Squamous Cell Carcinoma of Head and Neck; Acute Pain; Arthralgia; Arthritis, Gouty; Arthritis, Rheumatoid; Cardiovascular Diseases; Ductus Arteriosus, Patent; Eye Diseases; Myalgia; Osteoarthritis; Rheumatic Diseases; Spondylitis; Spondylitis, Ankylosing
Cyclooxygenase inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Progesterone receptor agonist
Small molecule
Approved
OTHER
ORAL
Inflammatory Bowel Diseases; Leukemia, Biphenotypic, Acute; Neoplasms, Plasma Cell; Osteoarthritis; Small Cell Lung Carcinoma; Tuberculosis; Angina, Stable; Diabetes Mellitus; Essential Hypertension; Fallopian Tube Neoplasms; Hand-Foot Syndrome; Heart Failure; Kidney Calculi; Leishmaniasis; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myeloid, Acute; Liver Cirrhosis; Metabolic Syndrome; Multiple Myeloma; Myelodysplastic Syndromes; Myeloproliferative Disorders; Ovarian Neoplasms; Peritoneal Neoplasms; Renal Insufficiency, Chronic; Bipolar Disorder; Brain Diseases; Cardiovascular Diseases; Colitis, Ulcerative; Diabetes Mellitus, Type 2; Heart Diseases; Hernias, Diaphragmatic, Congenital; Hypertension; Hyperuricemia; Lymphoma, Non-Hodgkin; Obesity; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Sprains and Strains; Tumor Lysis Syndrome; Wounds and Injuries; Gout; Leukemia; Lymphoma; Neoplasms; Response Evaluation Criteria in Solid Tumors
Xanthine dehydrogenase inhibitor
Small molecule
Approved
OTHER
INJECTION; ORAL
Anemia, Sickle Cell; Diabetes Mellitus; Edema; Leukemia; Leukemia, Myeloid, Acute; Melanoma; Premature Birth; Schizophrenia; Acute Kidney Injury; Acute Lung Injury; Bronchopulmonary Dysplasia; Dyspnea; Hypertension, Pregnancy-Induced; Keratosis, Actinic; Nasal Polyps; Neoplasms; Non-alcoholic Fatty Liver Disease; Prostatic Neoplasms; Renal Insufficiency, Chronic; Atherosclerosis; Bronchiolitis; Coronary Disease; Diabetes Mellitus, Type 2; Essential Hypertension; Hypercholesterolemia; Kidney Calculi; Kidney Diseases; Lung Diseases; Myocardial Infarction; Pre-Eclampsia; Pulmonary Disease, Chronic Obstructive; Pulmonary Embolism; Renal Insufficiency; Tachypnea; Warts; Cardiovascular Diseases; Fibrosis; Heart Failure; Hypertension; Liver Cirrhosis; Nephrotic Syndrome; Pulmonary Edema; Syndrome
Sodium-(potassium)-chloride cotransporter 2 inhibitor
Small molecule
Approved
OTHER
ORAL
Lymphoma, Non-Hodgkin; Glioblastoma; Histiocytosis, Langerhans-Cell; Hodgkin Disease; Anemia, Refractory; Anemia, Refractory, with Excess of Blasts; Brain Neoplasms; Central Nervous System Neoplasms; Leukemia; Leukemia, Basophilic, Acute; Leukemia, Biphenotypic, Acute; Leukemia, Erythroblastic, Acute; Leukemia, Lymphoid; Leukemia, Megakaryoblastic, Acute; Leukemia, Monocytic, Acute; Leukemia, Myeloid, Acute; Leukemia, Myelomonocytic, Acute; Leukemia, Myelomonocytic, Chronic; Lymphoma; Myelodysplastic Syndromes; Myeloproliferative Disorders; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Neoplasms
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Polycythemia Vera; Neoplasms
DNA inhibitor