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Total: 6532
Small molecule
Approved
Unknown
INHALATION
Anxiety; Bell Palsy; Hypoxia; Lung Diseases; Neuralgia; Retinitis Pigmentosa; Autistic Disorder; Brain Diseases; Carcinoma, Non-Small-Cell Lung; Central Nervous System Neoplasms; Diabetes Mellitus, Type 2; Erectile Dysfunction; Ileus; Ischemia; Osteonecrosis; Reperfusion Injury; Respiratory Insufficiency; Angina, Stable; Brain Concussion; Brain Injuries; Breast Neoplasms; Carcinoma, Squamous Cell; Child Development Disorders, Pervasive; Colitis, Ulcerative; Death, Sudden, Cardiac; Endocarditis; Gliosarcoma; Idiopathic Pulmonary Fibrosis; Ischemic Stroke; Laryngeal Neoplasms; Lymphedema; Migraine Disorders; Multiple Myeloma; Myocardial Infarction; Neoplasms; Opioid-Related Disorders; Osteoradionecrosis; Pulmonary Fibrosis; Severe Acute Respiratory Syndrome; Sleep Apnea, Obstructive; Status Asthmaticus; Stress Disorders, Post-Traumatic; Stroke; Tinea Pedis; Tonsillitis; Urinary Tract Infections; Wounds and Injuries; Xerostomia; Acute Kidney Injury; Anemia, Sickle Cell; Bronchiolitis; Burns; Complex Regional Pain Syndromes; Coronary Disease; Diabetes Mellitus; Heart Failure; Hypertension, Pulmonary; Infections; Optic Neuropathy, Ischemic; Pain; Pneumonia; Postoperative Nausea and Vomiting; Pregnancy; Premature Birth; Pulmonary Disease, Chronic Obstructive; Pulmonary Embolism; Respiratory Distress Syndrome; Retinopathy of Prematurity; Schizophrenia; Sepsis; Ulcer; Vascular Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoma, Renal Cell; HIV Infections; Leukemia, Myeloid, Acute; Lupus Nephritis; Lymphoma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Triple Negative Breast Neoplasms; Anemia, Hemolytic, Autoimmune; Hematologic Neoplasms; Leukemia; Lymphoma, Follicular; Lymphoma, Mantle-Cell; Purpura, Thrombocytopenic, Idiopathic; Renal Insufficiency, Chronic; Waldenstrom Macroglobulinemia; Amyloidosis, Familial; Multiple Myeloma; Plasmacytoma; Neoplasms
26S proteasome inhibitor
Small molecule
Approved
Unknown
Unknown
Hepatitis B, Chronic; Infections; Renal Insufficiency, Chronic; Hepatitis C; Hepatitis C, Chronic; Severe Acute Respiratory Syndrome; Virus Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Cystic Fibrosis
Cystic fibrosis transmembrane conductance regulator stabiliser
Small molecule
Approved
Unknown
INHALATION
Bipolar Disorder; Depressive Disorder, Major; Cystic Fibrosis; Severe Acute Respiratory Syndrome; Death, Sudden, Cardiac; Heart Failure; Obsessive-Compulsive Disorder; Pulmonary Disease, Chronic Obstructive; Reperfusion Injury; Stress Disorders, Post-Traumatic; Tinea Pedis; Burns; Colorectal Neoplasms; Keratosis, Actinic; Respiratory Insufficiency
Unknown
Small molecule
Unknown
Unknown
Unknown
Hepatitis C, Chronic
Nonstructural protein 5A inhibitor
Small molecule
Approved
Unknown
Unknown
Bacterial Infections; Renal Insufficiency; Systemic Inflammatory Response Syndrome; Urinary Tract Infections; Infections; Pneumonia; Pyelonephritis
Unknown
Small molecule
Approved
Unknown
Unknown
Esophageal Neoplasms; Graft vs Host Disease; Liver Diseases; Ovarian Neoplasms; Pancreatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Breast Neoplasms; Carcinoma, Basal Cell; Leukemia; Medulloblastoma; Multiple Myeloma; Neoplasms
Unknown
Small molecule
Approved
Unknown
SUBCUTANEOUS
Obesity; Neurofibroma; Lipoma
Cell membrane disrupting agent
Small molecule
Approved
Unknown
Unknown
Hyperkalemia
Potassium chelating agent
Small molecule
Approved
Unknown
ORAL
Hepatitis B, Chronic; HIV Infections
Human immunodeficiency virus type 1 reverse transcriptase inhibitor
Small molecule
Approved
Unknown
Unknown
Amyotrophic Lateral Sclerosis; Insulin Resistance; Hepatitis D; Leukemia, Lymphocytic, Chronic, B-Cell; Acquired Immunodeficiency Syndrome; Hepatitis B, Chronic; HIV Infections; Severe Acute Respiratory Syndrome; Virus Diseases
Human immunodeficiency virus type 1 reverse transcriptase inhibitor
Small molecule
Approved
OTHER
INTRAVENOUS
Renal Insufficiency; Anemia, Iron-Deficiency; Renal Insufficiency, Chronic
Supplement
Small molecule
Unknown
Unknown
Unknown
Glioblastoma; Glioma; Liver Diseases; Carcinoma, Non-Small-Cell Lung; Neoplasms
Unknown
Small molecule
Approved
Unknown
INHALATION
Status Asthmaticus; Pulmonary Disease, Chronic Obstructive
Unknown
Small molecule
Approved
Unknown
ORAL
Heart Failure, Diastolic; Heart Failure, Systolic; Hypotension; Lymphoma; Multiple Organ Failure; Non-ST Elevated Myocardial Infarction; Aging; Angina, Stable; Atrial Fibrillation; Coronary Disease; Diabetic Nephropathies; Heart Failure; Hypotension, Orthostatic; Mitral Valve Stenosis; Neoplasms; Shock, Septic; Tachycardia; Cardiovascular Diseases
Potassium/sodium hyperpolarization-activated cyclic nucleotide-gated channel 4 blocker
Small molecule
Approved
Unknown
ORAL
Prostatic Neoplasms; Sexual Dysfunction, Physiological; Sexual Dysfunctions, Psychological
Unknown
Small molecule
Approved
Unknown
Unknown
Postoperative Nausea and Vomiting; Nausea
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Irritable Bowel Syndrome
Mu opioid receptor agonist
Small molecule
Approved
Unknown
ORAL
Familial Primary Pulmonary Hypertension; Hypertension, Pulmonary; Pulmonary Arterial Hypertension; Thrombosis
Prostanoid IP receptor agonist
Small molecule
Approved
Unknown
Unknown
Adenocarcinoma; Adenocarcinoma of Lung; Carcinoma; Carcinoma, Squamous Cell; Colorectal Neoplasms; Glioblastoma; Lung Neoplasms; Carcinoma, Non-Small-Cell Lung; Neoplasms
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
ORAL
Melanoma
Dual specificity mitogen-activated protein kinase kinase 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Child Development Disorders, Pervasive; Anxiety Disorders; Bipolar Disorder; Depressive Disorder; Depressive Disorder, Major; Schizophrenia; Psychotic Disorders
Unknown
Small molecule
Approved
Unknown
INTRAVENOUS
Leukemia, Lymphocytic, Chronic, B-Cell; Sarcoma, Ewing; Breast Neoplasms; Chondrosarcoma, Mesenchymal; Endocrine Gland Neoplasms; Fallopian Tube Neoplasms; Hereditary Breast and Ovarian Cancer Syndrome; Liposarcoma, Myxoid; Meningioma; Mesothelioma; Pancreatic Neoplasms; Peritoneal Neoplasms; Prostatic Neoplasms, Castration-Resistant; Soft Tissue Neoplasms; Ovarian Neoplasms; Sarcoma; Leiomyosarcoma; Liposarcoma; Neoplasms
DNA inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Cholangiocarcinoma; Colorectal Neoplasms
Unknown
Small molecule
Approved
Unknown
ORAL
Gout; Hyperuricemia
Solute carrier family 22 member 12 inhibitor
Small molecule
Unknown
Unknown
Unknown
Carcinoma, Pancreatic Ductal; Esophageal Neoplasms; Leukemia, Myeloid, Acute; Multiple Myeloma; Sarcoma; Skin Neoplasms; Stomach Neoplasms; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Cholangiocarcinoma; Craniopharyngioma; Leukemia, Myelomonocytic, Chronic; Ovarian Neoplasms; Thyroid Neoplasms; Colorectal Neoplasms; Melanoma; Neoplasms
Dual specificity mitogen-activated protein kinase kinase 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Anemia, Sickle Cell; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Colonic Neoplasms; HIV Infections; Leukemia, Myelomonocytic, Chronic; Liver Neoplasms; Lung Neoplasms; Lymphoma, Mantle-Cell; Melanoma; Nasopharyngeal Neoplasms; Polycythemia Vera; Primary Myelofibrosis; Prostatic Neoplasms; Rectal Neoplasms; Skin Neoplasms; Breast Neoplasms; Carcinoma, Renal Cell; Colorectal Neoplasms; Diffuse Intrinsic Pontine Glioma; Glioblastoma; Glioma; Graft vs Host Disease; Hematologic Neoplasms; Leukemia; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Leukemia, Plasma Cell; Lymphoma; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Cutaneous; Myelodysplastic Syndromes; Neuroendocrine Tumors; Pancreatic Neoplasms; Plasmacytoma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms, Castration-Resistant; Stomach Neoplasms; Thyroid Neoplasms; Waldenstrom Macroglobulinemia; Hodgkin Disease; Multiple Myeloma; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Lymphoma; Ovarian Neoplasms; Prostatic Neoplasms, Castration-Resistant; Rectal Neoplasms; Adenocarcinoma; Adenocarcinoma, Follicular; Adenocarcinoma of Lung; Biliary Tract Neoplasms; Breast Neoplasms; Carcinoma, Adenoid Cystic; Carcinoma, Merkel Cell; Carcinoma, Neuroendocrine; Cholangiocarcinoma; Glioma; Meningeal Carcinomatosis; Mesothelioma; Neuroendocrine Tumors; Osteosarcoma; Sarcoma; Small Cell Lung Carcinoma; Stomach Neoplasms; Uterine Cervical Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Carcinoma, Renal Cell; Carcinoma, Squamous Cell; Colorectal Neoplasms; Endometrial Neoplasms; Esophageal Neoplasms; Melanoma; Urinary Bladder Neoplasms; Neoplasms; Thyroid Neoplasms
Unknown
Small molecule
Approved
Unknown
ORAL
Carcinoma, Ductal; Carcinoma, Pancreatic Ductal; Glioblastoma; Head and Neck Neoplasms; Hereditary Breast and Ovarian Cancer Syndrome; Kidney Diseases; Leukemia, Myeloid, Acute; Lung Neoplasms; Lymphoma, Non-Hodgkin; Multiple Myeloma; Pancreatic Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Adenocarcinoma; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Chordoma; Colonic Neoplasms; Endometrial Neoplasms; Liposarcoma; Lymphoma; Lymphoma, Mantle-Cell; Melanoma; Nasopharyngeal Neoplasms; Neuroendocrine Tumors; Oligodendroglioma; Ovarian Neoplasms; Prostatic Neoplasms, Castration-Resistant; Sarcoma, Ewing; Thymus Neoplasms; Urinary Bladder Neoplasms; Carcinoma, Squamous Cell; Sarcoma; Breast Neoplasms; Neoplasms
CDK6/cyclin D1 inhibitor
Small molecule
Approved
Unknown
Unknown
Blood Coagulation Disorders; Hemorrhage; Ischemic Stroke; Peripheral Arterial Disease; Aortic Valve Stenosis; Atrial Fibrillation; Heart Diseases; Severe Acute Respiratory Syndrome; Stroke; Venous Thromboembolism; Thrombosis
Unknown
Small molecule
Approved
Unknown
ORAL
Cholestasis; Obesity; Smith-Lemli-Opitz Syndrome; Barrett Esophagus; Diarrhea; Fatty Liver; Lipodystrophy, Familial Partial; Liver Cirrhosis, Biliary; Non-alcoholic Fatty Liver Disease; Liver Diseases; Peroxisomal Disorders
Unknown
Small molecule
Approved
Unknown
INTRAVENOUS
Acute Coronary Syndrome; Coronary Disease; ST Elevation Myocardial Infarction; Ischemia; Thrombosis
Unknown
Small molecule
Approved
Unknown
INTRAMUSCULAR
Psychotic Disorders; Autistic Disorder; Bipolar Disorder; Depressive Disorder, Major; Schizophrenia; Tourette Syndrome
Dopamine D2 receptor partial agonist