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Total: 6532
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Neoplasms; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes
Cytidine deaminase inhibitor
Small molecule
Approved
Unknown
Unknown
Dwarfism, Pituitary
Growth hormone receptor agonist
Small molecule
Approved
Unknown
Unknown
Lice Infestations
Copper sequestering agent
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease; Chronic Traumatic Encephalopathy; Cognitive Dysfunction
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Severe Acute Respiratory Syndrome; Colitis, Ulcerative; Crohn Disease; Multiple Sclerosis; Immune System Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung
Hepatocyte growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
HIV Infections; Virus Diseases
Envelope polyprotein GP160 inhibitor
Small molecule
Approved
Unknown
Unknown
Alopecia; Acne Vulgaris
Androgen Receptor antagonist
Small molecule
Approved
Unknown
Unknown
Anorexia Nervosa; Depressive Disorder, Major; Obsessive-Compulsive Disorder; Renal Insufficiency, Chronic; Bipolar Disorder; Nausea; Anxiety; Dementia; Depressive Disorder; Schizophrenia; Postoperative Nausea and Vomiting; Psychotic Disorders
Dopamine receptors; D2 & D3 antagonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Epilepsies, Partial; Epilepsy; Seizures
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Parkinson Disease
Catechol O-methyltransferase inhibitor
Small molecule
Approved
Unknown
Unknown
Constipation
Osmotic agent
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Central Nervous System Neoplasms; Colorectal Neoplasms; Gliosarcoma; Head and Neck Neoplasms; Lymphoma; Breast Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Liver Neoplasms; Ovarian Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Carcinoma, Non-Small-Cell Lung; Hepatitis D; Leukemia, Myelomonocytic, Chronic; Myelodysplastic Syndromes; Neoplasm Metastasis; Progeria
Protein farnesyltransferase inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Cushing Syndrome; Essential Hypertension; Hyperaldosteronism; Hypertension; Pituitary ACTH Hypersecretion; Adrenal Gland Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Hypertension; Irritable Bowel Syndrome; Urinary Bladder, Overactive; Urinary Incontinence; Urinary Incontinence, Urge
Beta-3 adrenergic receptor agonist
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Sleep Apnea, Obstructive; Sleep Disorders, Circadian Rhythm; Sleep Initiation and Maintenance Disorders
Orexin receptor 1 antagonist
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Biliary Tract Neoplasms; Cholangiocarcinoma; Colonic Neoplasms; Kidney Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Optic Nerve Glioma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Sarcoma, Kaposi; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Adenocarcinoma; Adenocarcinoma, Follicular; Breast Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Squamous Cell; Colorectal Neoplasms; Gallbladder Neoplasms; Liver Neoplasms; Lung Neoplasms; Lymphoma, Large B-Cell, Diffuse; Melanoma; Multiple Myeloma; Neurofibroma, Plexiform; Neurofibromatosis 1; Pancreatic Neoplasms; Sarcoma; Stomach Neoplasms; Carcinoma, Non-Small-Cell Lung; Thyroid Neoplasms; Neoplasms
Dual specificity mitogen-activated protein kinase kinase 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Glycogen Storage Disease Type I; Migraine Disorders; Amyotrophic Lateral Sclerosis; Ataxia Telangiectasia; Glycogen Storage Disease; Glycogen Storage Disease Type VII; Hemiplegia; Huntington Disease; Rett Syndrome
Supplement
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Serotonin 1f (5-HT1f) receptor agonist
Small molecule
Unknown
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung
Unknown
Small molecule
Approved
Unknown
Unknown
Diabetic Nephropathies; Heart Failure; Renal Insufficiency, Chronic
Mineralocorticoid receptor antagonist
Small molecule
Unknown
Unknown
Unknown
Cholangiocarcinoma
Fibroblast growth factor receptor inhibitor
Small molecule
Unknown
Unknown
Unknown
Bipolar Disorder; Schizophrenia
Delta opioid receptor partial agonist
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Cholangiocarcinoma; Carcinoma, Hepatocellular; Colorectal Neoplasms; Fallopian Tube Neoplasms; Glioblastoma; Ovarian Neoplasms; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Carcinoma, Renal Cell; Neoplasms
Vascular endothelial growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Alagille Syndrome; Biliary Atresia; Liver Diseases
Ileal bile acid transporter inhibitor
Small molecule
Unknown
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Cholestasis; Liver Cirrhosis, Biliary; Non-alcoholic Fatty Liver Disease; Alagille Syndrome; Biliary Atresia; Cholestasis, Intrahepatic; Pruritus
Ileal bile acid transporter inhibitor
Small molecule
Unknown
Unknown
Unknown
Liver Diseases; Graft vs Host Disease; Idiopathic Pulmonary Fibrosis; Psoriasis; Scleroderma, Diffuse
Rho-associated protein kinase 2 inhibitor
Small molecule
Unknown
Unknown
Unknown
Attention Deficit Disorder with Hyperactivity
Dopamine transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Gastrointestinal Stromal Tumors; Uterine Cervical Neoplasms; Achondroplasia; Glioblastoma; Melanoma; Neoplasms; Osteomalacia; Papillomavirus Infections; Squamous Cell Carcinoma of Head and Neck; Cholangiocarcinoma; Urinary Bladder Neoplasms
Fibroblast growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Hodgkin Disease; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Waldenstrom Macroglobulinemia
Unknown
Small molecule
Unknown
Unknown
Unknown
Candidiasis, Vulvovaginal
1,3-beta-glucan synthase inhibitor
Small molecule
Unknown
Unknown
Unknown
Small Cell Lung Carcinoma
Cyclin-dependent kinase 4 inhibitor