Small molecule
Approved
Unknown
Unknown
Anemia, Sickle Cell; Barrett Esophagus; Cardiovascular Diseases; Diabetic Retinopathy; Pulmonary Disease, Chronic Obstructive; Thoracic Neoplasms; Anxiety Disorders; Breast Carcinoma In Situ; Depressive Disorder, Major; Diabetes Insipidus; Head and Neck Neoplasms; HIV Infections; Li-Fraumeni Syndrome; Liver Diseases; Multiple Sclerosis; Muscular Dystrophy, Duchenne; Neuralgia; Osteoarthritis; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Sleep Apnea, Obstructive; Adenocarcinoma; Adenocarcinoma, Bronchiolo-Alveolar; Adenocarcinoma of Lung; Adenomatous Polyposis Coli; Aortic Aneurysm, Abdominal; Arthritis, Rheumatoid; Atrial Fibrillation; Bardet-Biedl Syndrome; Blindness; Breast Neoplasms; Burns; Carcinoma; Carcinoma, Hepatocellular; Carcinoma, Large Cell; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Cerebral Palsy; Colitis, Ulcerative; Colonic Neoplasms; Diabetic Foot; Endometrial Hyperplasia; Esophageal Neoplasms; Fragile X Syndrome; Frontotemporal Dementia; Geographic Atrophy; Glioblastoma; Heart Failure, Systolic; Hemangiosarcoma; Hepatitis; HIV-Associated Lipodystrophy Syndrome; Hypertension, Pulmonary; Intellectual Disability; Leukemia, Lymphocytic, Chronic, B-Cell; Low Back Pain; Lung Neoplasms; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Melanoma; Multiple Myeloma; Neoplasms; Neurobehavioral Manifestations; Neuroendocrine Tumors; Non-alcoholic Fatty Liver Disease; Ovarian Neoplasms; Pancreatic Neoplasms; Periodontitis; Peripheral Nervous System Diseases; Pregnancy; Prostatic Neoplasms; Rectal Neoplasms; Renal Insufficiency, Chronic; Severe Acute Respiratory Syndrome; Sex Chromosome Disorders of Sex Development; Small Cell Lung Carcinoma; Squamous Cell Carcinoma of Head and Neck; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Urogenital Neoplasms; Uterine Cervical Neoplasms; Weight Gain; Aging; Atherosclerosis; Bipolar Disorder; Brain Neoplasms; Cognitive Dysfunction; Colorectal Neoplasms; Coronary Disease; Diabetes, Gestational; Diabetes Mellitus, Type 1; Diabetes Mellitus, Type 2; Endometrial Neoplasms; Fatty Liver; Glucose Intolerance; Hidradenitis Suppurativa; Huntington Disease; Hypercholesterolemia; Hypertension; Infertility; Insulin Resistance; Lipid Metabolism Disorders; Liver Neoplasms; Metabolic Diseases; Metabolic Syndrome; Migraine Disorders; Muscular Dystrophies; Obesity; Peripheral Arterial Disease; Polycystic Kidney, Autosomal Dominant; Polycystic Ovary Syndrome; Prediabetic State; Prostatic Neoplasms, Castration-Resistant; Psoriasis; Psychotic Disorders; Schizophrenia; Diabetes Mellitus
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