Display Options:
Total: 6532
Small molecule
Approved
Unknown
Unknown
Neoplasms; Thyroid Neoplasms; Carcinoma, Medullary; Carcinoma, Non-Small-Cell Lung
Coiled-coil domain-containing protein 6/Tyrosine-protein kinase receptor RET inhibitor
Small molecule
Approved
Unknown
Unknown
Diabetes Mellitus, Type 2; Hypercholesterolemia; Lipid Metabolism Disorders; Hyperlipidemias; Atherosclerosis; Cardiovascular Diseases; Coronary Artery Disease; Hyperlipoproteinemia Type II
ATP-citrate synthase inhibitor
Small molecule
Approved
Unknown
Unknown
Psoriasis; Trigeminal Neuralgia; Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Angioedemas, Hereditary
Unknown
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Hepatocellular; Friedreich Ataxia; Neoplasms; Colorectal Neoplasms; Crohn Disease; Severe Acute Respiratory Syndrome; Cytomegalovirus Infections; Fever; Malaria, Falciparum; Malaria, Vivax; Schistosomiasis; Schistosomiasis haematobia; Malaria
Unknown
Small molecule
Approved
Unknown
Unknown
Pain
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease
Unknown
Small molecule
Approved
Unknown
Unknown
Glioma; Leukemia, Mast-Cell; Mastocytosis, Systemic; Gastrointestinal Stromal Tumors; Neoplasms
Platelet-derived growth factor receptor alpha inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Liver Diseases; Hemangiosarcoma; Brain Neoplasms; Breast Neoplasms; Neoplasms
Receptor protein-tyrosine kinase erbB-2 inhibitor
Small molecule
Approved
Unknown
Unknown
Pneumonia, Viral; Hemorrhagic Fever, Ebola; Respiratory Distress Syndrome; Severe Acute Respiratory Syndrome
Replicase polyprotein 1ab inhibitor
Small molecule
Approved
Unknown
ORAL
Multiple Sclerosis, Relapsing-Remitting; Multiple Sclerosis
Kelch-like ECH-associated protein 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Leukemia, Myeloid, Acute; Lymphoma; Prostatic Neoplasms, Castration-Resistant; Keratosis, Actinic
Tyrosine-protein kinase SRC inhibitor
Small molecule
Approved
Unknown
Unknown
Gastrointestinal Stromal Tumors; Neoplasms
Platelet-derived growth factor receptor alpha inhibitor
Small molecule
Approved
Unknown
Unknown
Pain; Acute Pain
Mu opioid receptor agonist
Small molecule
Unknown
Unknown
Unknown
Angioedemas, Hereditary
Plasma kallikrein inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoid Tumor; Endometrial Neoplasms; Glioblastoma; Leukemia; Stomach Neoplasms; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Mesothelioma; Sarcoma; Ovarian Neoplasms; Neoplasms; Small Cell Lung Carcinoma
DNA negative modulator
Small molecule
Unknown
Unknown
Unknown
Liver Diseases; Substance-Related Disorders; Precursor Cell Lymphoblastic Leukemia-Lymphoma
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Multiple Sclerosis
Sphingosine 1-phosphate receptor Edg-1 modulator
Small molecule
Approved
Unknown
ORAL
Substance-Related Disorders; Migraine Disorders
Serotonin 1f (5-HT1f) receptor agonist
Small molecule
Approved
Unknown
Unknown
Endometriosis; Leiomyoma; Pain; Prostatic Neoplasms, Castration-Resistant; Prostatic Neoplasms
Gonadotropin-releasing hormone receptor antagonist
Small molecule
Approved
Unknown
Unknown
Atrophy; Muscular Atrophy, Spinal
SMN2 pre-mRNA positive modulator
Small molecule
Unknown
Unknown
Unknown
Carcinoma, Medullary; Carcinoma, Non-Small-Cell Lung; Thyroid Neoplasms
Coiled-coil domain-containing protein 6/Tyrosine-protein kinase receptor RET inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Leukemia, Myeloid, Acute; Endometrial Neoplasms; Myeloproliferative Disorders; Urinary Bladder Neoplasms; Urogenital Neoplasms; Cholangiocarcinoma; Neoplasms
Fibroblast growth factor receptor 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Pituitary ACTH Hypersecretion
Cytochrome P450 11B1 inhibitor
Small molecule
Approved
Unknown
Unknown
Lymphoma, Follicular; Sarcoma
Histone-lysine N-methyltransferase EZH2 inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Autoimmune Diseases; HIV Infections
Envelope polyprotein GP160 inhibitor
Small molecule
Approved
Unknown
Unknown
Neuroblastoma; Trypanosomiasis, African; Chagas Disease; Leishmaniasis; Trypanosomiasis
DNA inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Glioblastoma; Liver Diseases; Carcinoma, Hepatocellular; Kidney Neoplasms; Lung Neoplasms; Melanoma; Carcinoma, Non-Small-Cell Lung; Sarcoma; Neoplasms
Hepatocyte growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Neoplasms; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes
Cytidine deaminase inhibitor